First CRISPR therapy editing genes inside the body nears FDA approval

A groundbreaking gene therapy using CRISPR technology could become the first to gain approval from the U.S. Food and Drug Administration for modifying genes directly inside a patient's body. Previous methods required extracting cells from the patient, editing them outside the body, and reinfusing them—a costly and complex process. The new approach eliminates this step, potentially simplifying treatment and reducing costs significantly.

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